Drug – bio-affecting and body treating compositions – Designated organic active ingredient containing – Radical -xh acid – or anhydride – acid halide or salt thereof...
Patent
1996-12-23
1998-05-12
O'Sullivan, Peter G.
Drug, bio-affecting and body treating compositions
Designated organic active ingredient containing
Radical -xh acid, or anhydride, acid halide or salt thereof...
514546, 514549, 514552, 514558, 514560, 514826, 514851, 560205, 560265, 562598, 562606, 562607, C07K 5326, C07K 53125, C07K 53122, A61K 3119
Patent
active
057505713
ABSTRACT:
Methods for treating cystic fibrosis are described. The methods involve the administration of a protein enhancing agent, differentiating agent and/or carboxy-compound to a subject afflicted with cystic fibrosis such that mutant cystic fibrosis transmembrane regulator protein present within cystic fibrosis-associated cells becomes functional. Other aspects described include therapeutic compositions and packaged drugs.
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Cheng Seng Hing
Fang Shaona Lee
Hoppe, IV Henry
Smith Alan Edward
Genzyme Corporation
O'Sullivan Peter G.
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