Methods and compositions for use in gene therapy for treatment o

Details Methods and compositions for use in gene therapy for treatment o Methods and compositions for use in gene therapy for treatment o

1998-03-12

2000-07-25

Schwartzman, Robert A.

Drug, bio-affecting and body treating compositions

Whole live micro-organism, cell, or virus containing

Genetically modified micro-organism, cell, or virus

424 936, 4353201, 435456, A61K 4800, C12N 1586

Patent

active

060933925

ABSTRACT:
The invention includes a composition comprising a recombinant adeno-associated viral vector comprising at least two adeno-associated virus inverted terminal repeats, a promoter/regulatory sequence, isolated DNA encoding Factor IX and accompanying 5' and 3' untranslated regions and a transcription termination signal, and methods of use thereof.

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